Ultragenyx

Journey

GTX-102 (apazunersen)

Currently enrolled in the GTX-102 study

Study timeline
You are here
  1. Enrollment

    May 8

  2. Baseline

    Jun 12

  3. Week 4

    Jul 24

  4. Week 8

    Aug 21

  5. Week 12

    Sep 18

  6. Bayley

    Oct 16

Program details

Study

GTX-102

Program

Angelman

Current week

Week 8

Observation

82%

Currently enrolled in the GTX-102 study.

Upcoming events

  1. Weekly Development Update

    Aug 28 · in 7 days

    Scheduled
  2. Bayley-4 Development Assessment

    Sep 04 · in 14 days

    Scheduled
  3. Follow-up Visit

    Sep 18 · in 28 days

    Scheduled

Post procedure check-in

After your recent lumbar puncture, tell us how you're feeling.

Safety & tolerability

Post-LP headache observations1 of 5 days
Back pain observations2 of 20 days
Observation completion94%

Observational reporting only. Clinical evaluation is performed by the study team.

Let your study team know if anything unusual happened.